معرفی
Ana Rita Batista is an Instructor in Neurology at UMass Chan Medical School, developing gene therapies for neurological disorders using AAV vectors. Her work focuses on optimizing CNS delivery and genetic correction strategies.
Education includes PhD in Biomedical Sciences and MSc in Biochemistry from University of Porto.
Research targets monogenic neurological conditions through advanced vector engineering. Recent studies demonstrate preclinical efficacy in movement disorder models and cognitive rehabilitation approaches. Key focus areas include blood-brain barrier crossing vectors and mutation-specific editing techniques.
Publications show progression from protein misfolding diseases to advanced CNS gene delivery platforms. Collaborations include work on Huntington's, muscular dystrophy, and enzyme deficiency disorders.
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- AAna Rita BatistaUniversity of Massachusetts Chan Medical School · پژوهشگر
Miguel Sena-EstevesUniversity of Massachusetts Chan Medical School · دانشیار- QQiushi TangUniversity of Massachusetts Chan Medical School · مدرس
Dan WangUniversity of Massachusetts Chan Medical School · استادیار- TToloo TaghianUniversity of Massachusetts Chan Medical School · مدرس
Allison May Keeler-KlunkUniversity of Massachusetts Chan Medical School · استادیار